Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE), a biopharmaceutical company focused on the development of novel products for rare and ultra-rare diseases, today announced presentations at two upcoming investor conferences. Tom Kassberg, the company’s Chief Business Officer, will be presenting at the Jefferies Autumn 2015 Global Healthcare Conference on Wednesday, November 18, 2015 at 8:40am GMT in London. Shalini Sharp, the company’s Chief Financial Officer, will be presenting at the Stifel 2015 Healthcare Conference on Wednesday, November 18, 2015 at 1:30pm ET in New York.

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FORUM Pharmaceuticals Inc., a biopharmaceutical company singularly focused on the development and delivery of transformative medicines to treat serious brain diseases, today announced that the U.S. Food and Drug Administration (FDA) has removed a partial clinical hold on the Phase 3 encenicline program for cognitive impairment in schizophrenia (CIS). This partial hold applied to a 26 week Phase 3 extension study. The two global Phase 3 efficacy and safety trials evaluating the use of encenicline to treat CIS are nearing completion, with top-line results anticipated in the first half of 2016.

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WuXi PharmaTech (Cayman) Inc. (NYSE:  WX) and Eli Lilly and Company (NYSE: LLY) today announced that they have entered into a strategic collaboration to develop, manufacture and commercialize a novel small molecule in China.

The potential medicine is a novel, once-daily oral agent, discovered by Lilly, which could address cardiovascular risk in patients with dyslipidemia, representing an unmet medical need worldwide. An estimated 276 million patients in China are affected by these conditions, including about 12 million patients requiring drug treatment. The potential medicine aims to reduce cardiovascular events in patients with elevated LDL cholesterol and triglycerides at high risk of cardiovascular events.

WuXi will be responsible for regulatory, development and manufacturing activities in China, which will be led and coordinated by WuXi’s Product Development Service and Partnership (PDSP) Business Unit. The potential medicine will be manufactured in China by WuXi to support China development. Lilly will be responsible for commercial activities. The parties will both invest in bringing this potential new medicine to patients in China. Further financial terms of the collaboration were not disclosed. An Investigational New Drug (IND) application will be filed in China by WuXi, and product development and registration will be carried out within China.

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Dimension Therapeutics, Inc. (NASDAQ:DMTX), a leading gene therapy company advancing novel, liver-directed treatments for diverse rare diseases, today announced its plans to expand the company’s internal research and process development capabilities. Dimension has signed a lease agreement with Alexandria Real Estate Equities, Inc. (NYSE:ARE) for 17,475 square feet of state-of-the-art laboratory and office space at 19 Presidential Way in Woburn, Massachusetts, with occupancy expected in April 2016. The expansion builds upon Dimension’s existing mammalian cell platform in Cambridge, and will support continued innovation in vector optimization and development of manufacturing processes required for IND-enabling studies and the reliable production of high quality AAV vectors at commercial scale.

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WuXi PharmaTech (Cayman) Inc. (NYSE:  WX), a leading open-access R&D capability and technology platform company serving the pharmaceutical, biotechnology, and medical device industries, today announced that its Laboratory Testing Division (LTD) has launched preclinical medical device testing services in China. These services are being offered for Chinese and international clients for their product registration with the China Food and Drug Administration (CFDA) and for Chinese clients for product registration in global markets.

LTD’s preclinical medical device testing services in China include a complete portfolio of biocompatibility, microbiology, and chemistry testing services. Major tests being offered include in vitro cytotoxicity; acute, sub-chronic and chronic toxicity; irritation; sensitization; hemocompatibility; implantation; genotoxicity; carcinogenicity; effects on reproduction, including development effects; extractable and leachable testing; and chemical characterization. WuXi has been a leader in providing preclinical and clinical medical device testing services in the United States for many years.

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Dimension Therapeutics, Inc. (“Dimension” or the “Company”), a leading gene therapy company advancing novel, liver-directed treatments for diverse rare diseases, today announced the pricing of its initial public offering of 5,500,000 shares of its common stock at a public offering price of $13.00 per share. Dimension’s underwriters have been granted a 30-day option to purchase up to an additional 825,000 shares of common stock at the public offering price less underwriting discounts and commissions. All shares in the offering will be sold by Dimension and are expected to begin trading on the NASDAQ Global Select Market on October 22, 2015 under the symbol “DMTX”.

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